Contact: Les Lang
University of North Carolina Health Care
Caption: This is R. Jude Samulski, PhD, University of North Carolina, a study senior author, professor of pharmacology and director of UNC's Gene Therapy Center. The treatment uses a virus (adeno-associated virus, or AAV) as a "viral vector" meticulously tailored to enter the brain and safely switch good genes for bad.
Credit: UNC School of Medicine
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