Contact: Hélène Puccio
INSERM (Institut national de la santé et de la recherche médicale)
Caption: The illustrations show a measurement of the activity of a mitochondrial protein (in blue) essential for cellular energy production, which is impaired when frataxin is absent (no staining in the untreated heart). Using gene therapy expressing frataxin, the activity of this essential protein can be corrected across the heart's entire surface.
Credit: © Inserm / H. Puccio
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