New Gene Therapy Method Improves Vision in Mice with Congenital Blindness (image)
Caption
Concepts of gene supplementation therapy and mutation replacement therapy. In gene supplementation therapy, new wildtype copies of the entire gene are added to the diseased cells. In mutation replacement therapy, mutation is locally excised and replaced with a wildtype sequence.
Credit
Koji Nishiguchi, Tohoku University Graduate School of Medicine
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Credit: Koji Nishiguchi, Tohoku University Graduate School of Medicine
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