Novel study at URI seeks to treat neurological symptoms of rare genetic disorder
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Updates every hour. Last Updated: 26-Dec-2025 17:11 ET (26-Dec-2025 22:11 GMT/UTC)
A rare, genetic disorder that affects bone marrow that prevents the production of healthy blood cells and platelets, usually leading to birth defects, blood disorders, and cancers in children and adolescents, has recently been discovered to also impact neurological health, prompting a novel study in the University of Rhode Island College of Pharmacy to search for treatments for Fanconi Anemia Neurological Syndrome.
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